Long-term follow-up of renal function in patients treated with migalastat for Fabry disease (vol 28, 100786, 2021)
Por:
Bichet, DG, Torra, R, Wallace, E, Hughes, D, Giugliani, R, Skuban, N, Krusinska, E, Feldt-Rasmussen, U, Schiffmann, R, Nicholls, K
Publicada:
1 dic 2021
Ahead of Print:
1 dic 2021
Resumen:
Filiaciones:
Bichet, DG:
Univ Montreal, Hop Sacre Coeur, Dept Med, Montreal, PQ, Canada
Torra, R:
Univ Autonoma Barcelona, IIB St Pau, Fundacio Puigvert, Inherited Renal Disorders,Nephrol Dept,REDINREN, Barcelona, Spain
Wallace, E:
Univ Alabama Birmingham, Dept Med, Birmingham, AL 35294 USA
Hughes, D:
Royal Free London NHS Fdn Trust, Lysosomal Storage Disorders Unit, London, England
UCL, London, England
Giugliani, R:
Univ Fed Rio Grande do Sul, Inst Biosci, Inst Basic Hlth Sci, Fac Med,Fac Pharm,Dept Genet,Med Genet Serv, Porto Alegre, RS, Brazil
Natl Inst Populat Med Genet INAGEMP, Porto Alegre, RS, Brazil
Skuban, N:
Amicus Therapeut Inc, Cranbury, NJ USA
Innocoll Pharmaceut, Newtown Sq, PA USA
Krusinska, E:
Amicus Therapeut Inc, Cranbury, NJ USA
Feldt-Rasmussen, U:
Univ Copenhagen, Natl Univ Hosp, Dept Med Endocrinol & Metab, Rigshosp, Copenhagen, Denmark
Schiffmann, R:
Baylor Scott & White Res Inst, Inst Metab Dis, Dallas, TX USA
Nicholls, K:
Univ Melbourne, Royal Melbourne Hosp, Dept Nephrol, Parkville, Vic, Australia
Green Published, gold
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