Long-term follow-up of renal function in patients treated with migalastat for Fabry disease (vol 28, 100786, 2021)


Por: Bichet, DG, Torra, R, Wallace, E, Hughes, D, Giugliani, R, Skuban, N, Krusinska, E, Feldt-Rasmussen, U, Schiffmann, R, Nicholls, K

Publicada: 1 dic 2021 Ahead of Print: 1 dic 2021
Resumen:


Filiaciones:
Bichet, DG:
 Univ Montreal, Hop Sacre Coeur, Dept Med, Montreal, PQ, Canada

Torra, R:
 Univ Autonoma Barcelona, IIB St Pau, Fundacio Puigvert, Inherited Renal Disorders,Nephrol Dept,REDINREN, Barcelona, Spain

Wallace, E:
 Univ Alabama Birmingham, Dept Med, Birmingham, AL 35294 USA

Hughes, D:
 Royal Free London NHS Fdn Trust, Lysosomal Storage Disorders Unit, London, England

 UCL, London, England

Giugliani, R:
 Univ Fed Rio Grande do Sul, Inst Biosci, Inst Basic Hlth Sci, Fac Med,Fac Pharm,Dept Genet,Med Genet Serv, Porto Alegre, RS, Brazil

 Natl Inst Populat Med Genet INAGEMP, Porto Alegre, RS, Brazil

Skuban, N:
 Amicus Therapeut Inc, Cranbury, NJ USA

 Innocoll Pharmaceut, Newtown Sq, PA USA

Krusinska, E:
 Amicus Therapeut Inc, Cranbury, NJ USA

Feldt-Rasmussen, U:
 Univ Copenhagen, Natl Univ Hosp, Dept Med Endocrinol & Metab, Rigshosp, Copenhagen, Denmark

Schiffmann, R:
 Baylor Scott & White Res Inst, Inst Metab Dis, Dallas, TX USA

Nicholls, K:
 Univ Melbourne, Royal Melbourne Hosp, Dept Nephrol, Parkville, Vic, Australia
ISSN: 22144269





Molecular Genetics and Metabolism Reports
Editorial
ELSEVIER, RADARWEG 29, 1043 NX AMSTERDAM, NETHERLANDS, Países Bajos
Tipo de documento: Correction
Volumen: 29 Número:
Páginas:
WOS Id: 000731336000001
ID de PubMed: 34934630
imagen Green Published, gold

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