CAR T-cells targeting FLT3 have potent activity against FLT3(-)ITD(+) AML and act synergistically with the FLT3-inhibitor crenolanib


Por: Jetani, H, Garcia-Cadenas, I, Nerreter, T, Thomas, S, Rydzek, J, Meijide, JB, Bonig, H, Herr, W, Sierra, J, Einsele, H, Hudecek, M

Publicada: 1 may 2018
Resumen:
FMS-like tyrosine kinase 3 (FLT3) is a transmembrane protein expressed on normal hematopoietic stem and progenitor cells (HSC) and retained on malignant blasts in acute myeloid leukemia (AML). We engineered CD8(+) and CD4(+) T-cells expressing a FLT3-specific chimeric antigen receptor (CAR) and demonstrate they confer potent reactivity against AML cell lines and primary AML blasts that express either wild-type FLT3 or FLT3 with internal tandem duplication (FLT3-ITD). We also show that treatment with the FLT3-inhibitor crenolanib leads to increased surface expression of FLT3 specifically on FLT3-ITD AML cells and consecutively, enhanced recognition by FLT3-CAR T-cells in vitro and in vivo. As anticipated, we found that FLT3-CAR T-cells recognize normal HSCs in vitro and in vivo, and disrupt normal hematopoiesis in colony formation assays, suggesting that adoptive therapy with FLT3-CAR T-cells will require subsequent CAR T-cell depletion and allogeneic HSC transplantation to reconstitute the hematopoietic system. Collectively, our data establish FLT3 as a novel CAR target in AML with particular relevance in high-risk FLT3-ITD AML. Further, our data provide the first proof of-concept that CAR T-cell immunotherapy and small molecule inhibition can be used synergistically, as exemplified by our data showing superior antileukemia efficacy of FLT3-CAR T-cells in combination with crenolanib.

Filiaciones:
Jetani, H:
 Univ Klinikum Wurzburg, Med Klin & Poliklin 2, Wurzburg, Germany

Garcia-Cadenas, I:
 Autonomous Univ Barcelona, St Pau & Jose Carreras Leukemia Res Inst, Hematol Dept, Hosp Santa Creu & St Pau, Barcelona, Spain

Nerreter, T:
 Univ Klinikum Wurzburg, Med Klin & Poliklin 2, Wurzburg, Germany

Thomas, S:
 Univ Klinikum Regensburg, Klin & Poliklin Innere Med 3, Regensburg, Germany

Rydzek, J:
 Univ Klinikum Wurzburg, Med Klin & Poliklin 2, Wurzburg, Germany

Meijide, JB:
 Autonomous Univ Barcelona, St Pau & Jose Carreras Leukemia Res Inst, Hematol Dept, Hosp Santa Creu & St Pau, Barcelona, Spain

Bonig, H:
 Goethe Univ Frankfurt, Inst Transfus Med & Immunhamatol, Frankfurt, Germany

 Deutsch Rotes Kreuz Blutspendedienst BaWuHe, Frankfurt, Germany

Herr, W:
 Univ Klinikum Regensburg, Klin & Poliklin Innere Med 3, Regensburg, Germany

Sierra, J:
 Autonomous Univ Barcelona, St Pau & Jose Carreras Leukemia Res Inst, Hematol Dept, Hosp Santa Creu & St Pau, Barcelona, Spain

Einsele, H:
 Univ Klinikum Wurzburg, Med Klin & Poliklin 2, Wurzburg, Germany

Hudecek, M:
 Univ Klinikum Wurzburg, Med Klin & Poliklin 2, Wurzburg, Germany
ISSN: 08876924





LEUKEMIA
Editorial
SPRINGERNATURE, CAMPUS, 4 CRINAN ST, LONDON, N1 9XW, ENGLAND, Reino Unido
Tipo de documento: Article
Volumen: 32 Número: 5
Páginas: 1168-1179
WOS Id: 000431769800012
ID de PubMed: 29472720

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