Digital Monitoring of Patients with Generalized Myasthenia Gravis: A Prospective Pilot Study


Por: Vesperinas, A, Rocaspana-Codana, J, Reyes-Leiva, D, Caballero-Avila, M, Carbayo, A, Collet-Vidiella, R, Llansó, L, Gallardo, E, Turon-Sans, J, Rojas-García, R, Cortés-Vicente, E

Publicada: 1 jun 2026 Ahead of Print: 1 abr 2026
Resumen:
Introduction: Monitoring patients with myasthenia gravis (MG) can be challenging due to the fluctuating nature of the disease. We aimed to test the reliability of using the MG Activities of Daily Living (MG-ADL) scale in the form of a smartphone application as a means for optimal patient monitoring and early exacerbation detection. Methods: We conducted an observational, prospective, single-center study including patients with generalized MG at risk of clinical worsening. Follow-up was based on routine outpatient visits, remote monitoring via weekly self-completion of the MG-ADL scale, and home visits by specialist nurses. Results: Thirty-one patients were included [41.9% female; mean (SD) age 59 (15) years], 87.1% seropositive for anti-AChR antibodies. MG-ADL scores reported by the patient via the application showed excellent agreement with healthcare provider scores (ICC = 0.92, P < 0.01), moderate correlation with the MG Composite scale (rho = 0.595, P < 0.01), and weak correlation with the Quantitative MG scale (rho = 0.328, P < 0.01). Over the 15-month follow-up period, compared to 23 exacerbations detected during routine outpatient visits, the application detected 38 exacerbations in 14 patients, 20 of which led to therapeutic modifications. Conclusion: This study demonstrates the reliability of MG-ADL scale data obtained via a smartphone application in reflecting clinical status and in detecting deterioration episodes sometimes missed during routine outpatient visits.

Filiaciones:
Vesperinas, A:
 Hosp Santa Creu i St Pau, Dept Neurol, Neuromuscular Dis Unit, C Pare Claret 167, Barcelona 08025, Spain

 Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain

 Univ Autonoma Barcelona, Dept Med, Barcelona, Spain

 Hosp Santa Creu I St Pau, Inst Recerca, Barcelona, Spain

Rocaspana-Codana, J:
 Hosp Santa Creu i St Pau, Dept Neurol, Neuromuscular Dis Unit, C Pare Claret 167, Barcelona 08025, Spain

 Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain

 Univ Autonoma Barcelona, Dept Med, Barcelona, Spain

 Hosp Santa Creu I St Pau, Inst Recerca, Barcelona, Spain

Reyes-Leiva, D:
 Hosp Santa Creu i St Pau, Dept Neurol, Neuromuscular Dis Unit, C Pare Claret 167, Barcelona 08025, Spain

 Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain

 Univ Autonoma Barcelona, Dept Med, Barcelona, Spain

 Hosp Santa Creu I St Pau, Inst Recerca, Barcelona, Spain

 Hosp St Joan Despi Moises Broggi, Barcelona, Spain

Caballero-Avila, M:
 Hosp Santa Creu i St Pau, Dept Neurol, Neuromuscular Dis Unit, C Pare Claret 167, Barcelona 08025, Spain

 Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain

 Univ Autonoma Barcelona, Dept Med, Barcelona, Spain

 Hosp Santa Creu I St Pau, Inst Recerca, Barcelona, Spain

Carbayo, A:
 Hosp Santa Creu i St Pau, Dept Neurol, Neuromuscular Dis Unit, C Pare Claret 167, Barcelona 08025, Spain

 Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain

 Univ Autonoma Barcelona, Dept Med, Barcelona, Spain

 Hosp Santa Creu I St Pau, Inst Recerca, Barcelona, Spain

Collet-Vidiella, R:
 Hosp Santa Creu i St Pau, Dept Neurol, Neuromuscular Dis Unit, C Pare Claret 167, Barcelona 08025, Spain

 Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain

 Univ Autonoma Barcelona, Dept Med, Barcelona, Spain

 Hosp Santa Creu I St Pau, Inst Recerca, Barcelona, Spain

Llansó, L:
 Hosp Santa Creu i St Pau, Dept Neurol, Neuromuscular Dis Unit, C Pare Claret 167, Barcelona 08025, Spain

 Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain

 Univ Autonoma Barcelona, Dept Med, Barcelona, Spain

 Hosp Santa Creu I St Pau, Inst Recerca, Barcelona, Spain

Gallardo, E:
 Hosp Santa Creu i St Pau, Dept Neurol, Neuromuscular Dis Unit, C Pare Claret 167, Barcelona 08025, Spain

 Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain

 Univ Autonoma Barcelona, Dept Med, Barcelona, Spain

 Hosp Santa Creu I St Pau, Inst Recerca, Barcelona, Spain

Turon-Sans, J:
 Hosp Santa Creu i St Pau, Dept Neurol, Neuromuscular Dis Unit, C Pare Claret 167, Barcelona 08025, Spain

 Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain

 Univ Autonoma Barcelona, Dept Med, Barcelona, Spain

 Hosp Santa Creu I St Pau, Inst Recerca, Barcelona, Spain

Rojas-García, R:
 Hosp Santa Creu i St Pau, Dept Neurol, Neuromuscular Dis Unit, C Pare Claret 167, Barcelona 08025, Spain

 Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain

 Univ Autonoma Barcelona, Dept Med, Barcelona, Spain

 Hosp Santa Creu I St Pau, Inst Recerca, Barcelona, Spain

Cortés-Vicente, E:
 Hosp Santa Creu i St Pau, Dept Neurol, Neuromuscular Dis Unit, C Pare Claret 167, Barcelona 08025, Spain

 Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain

 Univ Autonoma Barcelona, Dept Med, Barcelona, Spain

 Hosp Santa Creu I St Pau, Inst Recerca, Barcelona, Spain
ISSN: 21938253





Neurology and Therapy
Editorial
SPRINGER LONDON LTD, 236 GRAYS INN RD, 6TH FLOOR, LONDON WC1X 8HL, ENGLAND, Nueva Zelanda
Tipo de documento: Article
Volumen: 15 Número: 3
Páginas: 1345-1355
WOS Id: 001736490000001
ID de PubMed: 41957339
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