Targeting LDL aggregation decreases atherosclerotic lipid burden in a humanized mouse model of familial hypercholesterolemia: Crucial role of ApoB100 conformational stabilization


Por: Benitez-Amaro, A, Garcia, E, Lhoëst, MTL, Martínez, A, Borrás, C, Tondo, M, Céspedes, MV, Caruana, P, Pepe, A, Bochicchio, B, Cenarro, A, Civeira, F, Prades, R, Escola-Gil, JC, Llorente-Cortés, V

Publicada: 1 nov 2025 Ahead of Print: 1 nov 2025
Resumen:
Background and aims: Low-density lipoprotein (LDL) aggregation is nowadays considered a therapeutic target in atherosclerosis. DP3, the retro-enantio version of the sequence Gly1127-Cys1140 of LRP1, efficiently inhibits LDL aggregation and foam cell in vitro formation. Here, we investigate whether DP3 modulates atherosclerosis in a humanized ApoB100, LDL receptor (LDLR) knockout mice (Ldlr- /- hApoB100 Tg) and determine the potential LDL-related underlying mechanisms. Methods: Tg mice were fed an HFD for 21 days to induce atherosclerosis and then randomized into three groups that received a daily subcutaneous administration (10 mg/kg) of i) vehicle, ii) DP3 peptide, or iii) a non-active peptide (IP321). The in vivo biodistribution of a fluorescent-labeled peptide version (TAMRA-DP3), and its colocalization with ApoB100 in the arterial intima, was analyzed by imaging system (IVIS) and confocal microscopy. Heart aortic roots were used for atherosclerosis detection and quantification. LDL functionality was analyzed by biochemical, biophysical, molecular, and cellular studies. Results: Intimal neutral lipid accumulation in the aortic root was reduced in the DP3-treated group as compared to control groups. ApoB100 in LDLs from the DP3 group exhibited an increased percentage of alpha-helix secondary structures and decreased immunoreactivity to anti-ApoB100 antibodies. LDL from DP3-treated mice were protected against passive and sphingomyelinase (SMase)-induced aggregation, although they still experienced SMase-induced sphingomyelin phospholysis. In patients with familial hypercholesterolemia (FH), DP3 efficiently inhibited both SMase-induced phospholysis and aggregation. Conclusions: DP3 peptide administration inhibits atherosclerosis by preserving the alpha-helix secondary structures of ApoB100 in a humanized ApoB100 murine model that mimicks the hallmark of human hypercholesterolemia.

Filiaciones:
Benitez-Amaro, A:
 CSIC, Inst Biomed Res Barcelona, Barcelona 08036, Spain

 Inst Invest Biomed St Pau, Barcelona 08041, Spain

Garcia, E:
 CSIC, Inst Biomed Res Barcelona, Barcelona 08036, Spain

 Inst Invest Biomed St Pau, Barcelona 08041, Spain

 Univ Autonoma Barcelona, Barcelona 08193, Spain

Lhoëst, MTL:
 CSIC, Inst Biomed Res Barcelona, Barcelona 08036, Spain

 Inst Invest Biomed St Pau, Barcelona 08041, Spain

 Univ Autonoma Barcelona, Barcelona 08193, Spain

Martínez, A:
 CSIC, Inst Biomed Res Barcelona, Barcelona 08036, Spain

 Inst Invest Biomed St Pau, Barcelona 08041, Spain

Borrás, C:
 Inst Invest Biomed St Pau, Inst Recerca Hosp Santa Creu & St Pau, Barcelona 08041, Spain

 CIBER Diabet & Enfermedades Metab Asociadas, Madrid 28029, Spain

Tondo, M:
 CIBER Diabet & Enfermedades Metab Asociadas, Madrid 28029, Spain

 Hosp Santa Creu & Sant Pau, Dept Clin Biochem, Barcelona 08041, Spain

Céspedes, MV:
 Inst Recerca St Pau, Hosp Santa Creu & St Pau, Grup Oncol Ginecol & Peritoneal, Barcelona 08041, Spain

 Univ Barcelona, Barcelona 08007, Spain

Caruana, P:
 Inst Recerca St Pau, Hosp Santa Creu & St Pau, Grup Oncol Ginecol & Peritoneal, Barcelona 08041, Spain

 Univ Barcelona, Barcelona 08007, Spain

Pepe, A:
 Univ Basilicata, Dept Sci, Lab Bioinspired Mat, Potenza, Italy

Bochicchio, B:
 Univ Basilicata, Dept Sci, Lab Bioinspired Mat, Potenza, Italy

Cenarro, A:
 Univ Zaragoza, Hosp Univ Miguel Servet, IIS Arago, Inst Aragones Ciencias Salud, Zaragoza, Spain

 Inst Hlth Carlos III, CIBER Enfermedades Cardiovasc, Madrid 28029, Spain

Civeira, F:
 Univ Zaragoza, Hosp Univ Miguel Servet, IIS Arago, Inst Aragones Ciencias Salud, Zaragoza, Spain

 Inst Hlth Carlos III, CIBER Enfermedades Cardiovasc, Madrid 28029, Spain

Prades, R:
 Iproteos SL, Barcelona Sci Pk, Barcelona, Spain

Escola-Gil, JC:
 Inst Invest Biomed St Pau, Inst Recerca Hosp Santa Creu & St Pau, Barcelona 08041, Spain

 CIBER Diabet & Enfermedades Metab Asociadas, Madrid 28029, Spain

Llorente-Cortés, V:
 CSIC, Inst Biomed Res Barcelona, Barcelona 08036, Spain

 Inst Invest Biomed St Pau, Barcelona 08041, Spain

 Inst Hlth Carlos III, CIBER Enfermedades Cardiovasc, Madrid 28029, Spain
ISSN: 00219150





ATHEROSCLEROSIS
Editorial
ELSEVIER IRELAND LTD, ELSEVIER HOUSE, BROOKVALE PLAZA, EAST PARK SHANNON, CO, CLARE, 00000, IRELAND, Estados Unidos America
Tipo de documento: Article
Volumen: 410 Número:
Páginas:
WOS Id: 001622431600005
ID de PubMed: 39547850
imagen Green Submitted, hybrid

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