Long-term sex differences in atherosclerotic cardiovascular disease in individuals with heterozygous familial hypercholesterolaemia in Spain: a study using data from SAFEHEART, a nationwide, multicentre, prospective cohort study


Por: de Isla, LP, Vallejo-Vaz, AJ, Watts, GF, Muñiz-Grijalvo, O, Alonso, R, Diaz-Diaz, JL, Arroyo-Olivares, R, Aguado, R, Argueso, R, Mauri, M, Romero, MJ, Alvarez-Baños, P, Mañas, D, Cepeda, JM, Gonzalez-Bustos, P, Casañas, M, Michan, A, Muñoz-Torrero, JFS, Faedo, C, Barba, MA, Dieguez, M, de Andrés, R, Hernandez, AM, Gonzalez-Estrada, A, Padró, T, Fuentes, F, Badimon, L, Mata, P

Publicada: 1 sep 2024 Ahead of Print: 1 ago 2024
Resumen:
Background Sex differences in atherosclerotic cardiovascular disease (ASCVD) in familial hypercholesterolaemia have been reported but are not fully established. We aimed to assess sex differences in the risk of ASCVD and life-time burden of ASCVD in patients with heterozygous familial hypercholesterolaemia. Methods SAFEHEART is a nationwide, multicentre, long-term prospective cohort study conducted in 25 tertiary care hospitals and one regional hospital in Spain. Participants in the SAFEHEART study aged 18 years or older with genetically confirmed familial hypercholesterolaemia were included in our analysis. Data were obtained between Jan 26, 2004, and Nov 30, 2022. ASCVD and age at onset were documented at enrolment and at follow-up. Our aim was to investigate the differences by sex in the risk and burden of ASCVD in patients with heterozygous familial hypercholesterolaemia, over the study follow-up and over the life course. The SAFEHEART study is registered with ClinicalTrials.gov, NCT02693548. Findings Of the 5262 participants in SAFEHEART at the time of analysis, 3506 (1898 [541%] female and 1608 [459%] male participants) met the inclusion criteria and were included in the current study. Mean age was 461 years (SD 155) and median follow-up was 103 years (IQR 64-130). Mean on-treatment LDL-cholesterol at follow-up was 31 mmol/L (SD 14) in females and 30 mmol/L (15) in males. LDL-cholesterol reductions over time were similar in both sexes (139 mmol/L [95% CI 130-147] absolute reduction in females vs 139 mmol/L [129-148] in males; p=098). At enrolment, 130 (68%) females and 304 (189%) males (p<00001) had cardiovascular disease. During follow-up, 134 (71%) females and 222 (138%) males (p<00001) had incident cardiovascular events. Median age at first ASCVD event (mostly due to coronary artery disease) was 616 years (IQR 500-714) in females and 506 years (420-586) in males (p<00001). The adjusted hazard ratio for ASCVD in males compared with females during follow-up was 190 (95% CI 149-242) and for cardiovascular death was 174 (111-273). Major adverse cardiovascular disease event (MACE)-free survival from birth was lower in males than females (hazard ratio 352 [95% CI 298-416]; p<00001). Median MACE-free survival time was 901 years (95% CI 865-not estimable) in females and 710 years (692-746) in males. The age at which 25% of female participants have had a MACE event was 749 years, this figure was 555 years in male participants. Interpretation Our findings suggest that the burden and risk of ASCVD are markedly lower in females than males with familial hypercholesterolaemia. The impact of sex needs to be considered to improve risk stratification and personalised management in patients with heterozygous familial hypercholesterolaemia. Funding Fundaci & oacute;n Hipercolesterolemia Familiar, the Instituto de Salud Carlos III, and Next Generation EU funds from the Recovery and Resilience Mechanism Program. Copyright (c) 2024 Published by Elsevier Ltd. All rights reserved, including those for text and data mining, AI training, and similar technologies.

Filiaciones:
de Isla, LP:
 Univ Complutense, Hosp Clin San Carlos, Fac Med, Cardiol Dept, Madrid 28040, Spain

 Fdn Hipercolesterolemia Familiar, Madrid 28010, Spain

Vallejo-Vaz, AJ:
 Univ Seville, Fac Med, Dept Med, Seville, Spain

 Univ Seville, Clin Epidemiol & Vasc Risk, Inst Biomed Sevilla IBiS, IBiS,Hosp Univ Virgen del Rocio,CSIC, Seville, Spain

 Inst Salud Carlos III, Ctr Invest Biomed Red Epidemiol & Salud Publ, Madrid, Spain

Watts, GF:
 Univ Western Australia, Sch Med, Perth, WA, Australia

 Royal Perth Hosp, Dept Cardiol, Cardiometab Serv, Perth, WA, Australia

 Royal Perth Hosp, Dept Internal Med, Cardiometab Serv, Perth, WA, Australia

Muñiz-Grijalvo, O:
 Univ Seville, Clin Epidemiol & Vasc Risk, Inst Biomed Sevilla IBiS, IBiS,Hosp Univ Virgen del Rocio,CSIC, Seville, Spain

 Hosp Virgen del Rocio, Dept Internal Med, Seville, Spain

Alonso, R:
 Fdn Hipercolesterolemia Familiar, Madrid 28010, Spain

 Ctr Adv Metab Med & Nutr, Santiago, Chile

Diaz-Diaz, JL:
 Hosp Abente & Lago, Dept Internal Med, La Coruna, Spain

Arroyo-Olivares, R:
 Fdn Hipercolesterolemia Familiar, Madrid 28010, Spain

Aguado, R:
 Hosp Gen Leon, Dept Endocrinol, Leon, Spain

Argueso, R:
 Hosp Univ Lucus Augusti, Dept Endocrinol, Lugo, Spain

Mauri, M:
 Hosp Terrassa, Dept Internal Med, Terrassa, Spain

Romero, MJ:
 Hosp Infanta Elena, Dept Internal Med, Huelva, Spain

Alvarez-Baños, P:
 Hosp Univ Burgos, Dept Endocrinol, Burgos, Spain

Mañas, D:
 Hosp Univ Ciudad Real, Dept Internal Med, Ciudad Real, Spain

Cepeda, JM:
 Hosp Comarcal Vega Baja, Dept Internal Med, Orihuela, Spain

Gonzalez-Bustos, P:
 Hosp Univ Virgen de las Nieves, Dept Internal Med, Granada, Spain

Casañas, M:
 Hosp San Pedro, Dept Internal Med, Logrono, Spain

Michan, A:
 Hosp Jerez de la Frontera, Dept Internal Med, Jerez de la Frontera, Spain

Muñoz-Torrero, JFS:
 Hosp San Pedro de Alcantara, Dept Internal Med, Caceres, Spain

Faedo, C:
 Hosp Cent Asturias, Dept Endocrinol, Oviedo, Spain

Barba, MA:
 Complejo Hosp Univ Albacete, Dept Internal Med, Albacete, Spain

Dieguez, M:
 Hosp Cabuenes, Dept Endocrinol, Gijon, Spain

de Andrés, R:
 Fdn Jimenez Diaz, Dept Internal Med, Madrid, Spain

Hernandez, AM:
 Hosp Clin Univ Virgen de la Arrixaca, Dept Endocrinol, Murcia, Spain

Gonzalez-Estrada, A:
 Univ Seville, Clin Epidemiol & Vasc Risk, Inst Biomed Sevilla IBiS, IBiS,Hosp Univ Virgen del Rocio,CSIC, Seville, Spain

 Hosp Virgen del Rocio, Dept Internal Med, Seville, Spain

Padró, T:
 Hosp Santa Creu & Sant Pau, Res Inst, IIBSt Pau, CiberCV, Barcelona, Spain

Fuentes, F:
 Univ Cordoba, Lipids & Atherosclerosis Unit, CIBERObn, IMIBIC,Reina Sofia Univ Hosp, Cordoba, Spain

Badimon, L:
 Hosp Santa Creu & Sant Pau, Res Inst, IIBSt Pau, CiberCV, Barcelona, Spain

Mata, P:
 Fdn Hipercolesterolemia Familiar, Madrid 28010, Spain
ISSN: 22138587





Lancet Diabetes & Endocrinology
Editorial
ELSEVIER SCIENCE INC, STE 800, 230 PARK AVE, NEW YORK, NY 10169 USA, Reino Unido
Tipo de documento: Article
Volumen: 12 Número: 9
Páginas: 643-652
WOS Id: 001301849000001
ID de PubMed: 39098315

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