The Diphtheria Toxin Translocation Domain Impairs Receptor Selectivity in Cancer Cell-Targeted Protein Nanoparticles


Por: Volta-Duran, E, Sanchez, JM, Parlade, E, Serna, N, Vazquez, E, Unzueta, U, Villaverde, A

Publicada: 1 dic 2022
Resumen:
Protein-based materials intended as nanostructured drugs or drug carriers are progressively gaining interest in nanomedicine, since their structure, assembly and cellular interactivity can be tailored by recruiting functional domains. The main bottleneck in the development of deliverable protein materials is the lysosomal degradation that follows endosome maturation. This is especially disappointing in the case of receptor-targeted protein constructs, which, while being highly promising and in demand in precision medicines, enter cells via endosomal/lysosomal routes. In the search for suitable protein agents that might promote endosome escape, we have explored the translocation domain (TD) of the diphtheria toxin as a functional domain in CXCR4-targeted oligomeric nanoparticles designed for cancer therapies. The pharmacological interest of such protein materials could be largely enhanced by improving their proteolytic stability. The incorporation of TD into the building blocks enhances the amount of the material detected inside of exposed CXCR4(+) cells up to around 25-fold, in absence of cytotoxicity. This rise cannot be accounted for by endosomal escape, since the lysosomal degradation of the new construct decreases only moderately. On the other hand, a significant loss in the specificity of the CXCR4-dependent cellular penetration indicates the unexpected role of the toxin segment as a cell-penetrating peptide in a dose-dependent and receptor-independent fashion. These data reveal that the diphtheria toxin TD displayed on receptor-targeted oligomeric nanoparticles partially abolishes the exquisite receptor specificity of the parental material and it induces nonspecific internalization in mammalian cells.

Filiaciones:
Volta-Duran, E:
 Univ Autonoma Barcelona, Inst Biotecnol & Biomed, Barcelona 08193, Spain

 Inst Salud Carlos III, CIBER Bioingn, Biomat & Nanomed CIBER BBN, Barcelona 08193, Spain

 Univ Autonoma Barcelona, Dept Genet & Microbiol, Barcelona 08193, Spain

Sanchez, JM:
 Univ Autonoma Barcelona, Inst Biotecnol & Biomed, Barcelona 08193, Spain

 Inst Salud Carlos III, CIBER Bioingn, Biomat & Nanomed CIBER BBN, Barcelona 08193, Spain

 Univ Autonoma Barcelona, Dept Genet & Microbiol, Barcelona 08193, Spain

 Univ Nacl Cordoba, Inst Invest Biol & Tecnol IIBYT, CONICET, Ave Velez Sarsfield 1611,X5016GCA, Cordoba, Argentina

Parlade, E:
 Univ Autonoma Barcelona, Inst Biotecnol & Biomed, Barcelona 08193, Spain

 Inst Salud Carlos III, CIBER Bioingn, Biomat & Nanomed CIBER BBN, Barcelona 08193, Spain

 Univ Autonoma Barcelona, Dept Genet & Microbiol, Barcelona 08193, Spain

Serna, N:
 Univ Autonoma Barcelona, Inst Biotecnol & Biomed, Barcelona 08193, Spain

 Inst Salud Carlos III, CIBER Bioingn, Biomat & Nanomed CIBER BBN, Barcelona 08193, Spain

 Univ Autonoma Barcelona, Dept Genet & Microbiol, Barcelona 08193, Spain

 Univ Autonoma Barcelona, Nanoligent SL, Campus Univ, Barcelona 08193, Spain

Vazquez, E:
 Univ Autonoma Barcelona, Inst Biotecnol & Biomed, Barcelona 08193, Spain

 Inst Salud Carlos III, CIBER Bioingn, Biomat & Nanomed CIBER BBN, Barcelona 08193, Spain

 Univ Autonoma Barcelona, Dept Genet & Microbiol, Barcelona 08193, Spain

Unzueta, U:
 Inst Salud Carlos III, CIBER Bioingn, Biomat & Nanomed CIBER BBN, Barcelona 08193, Spain

 Univ Autonoma Barcelona, Dept Genet & Microbiol, Barcelona 08193, Spain

 Inst Invest Biomed St Pau IIB St PAU, St Quinti 77-79, Barcelona 08041, Spain

 Josep Carreras Leukaemia Res Inst, Barcelona 08025, Spain

Villaverde, A:
 Univ Autonoma Barcelona, Inst Biotecnol & Biomed, Barcelona 08193, Spain

 Inst Salud Carlos III, CIBER Bioingn, Biomat & Nanomed CIBER BBN, Barcelona 08193, Spain

 Univ Autonoma Barcelona, Dept Genet & Microbiol, Barcelona 08193, Spain
ISSN: 19994923
Editorial
MDPI, ST ALBAN-ANLAGE 66, CH-4052 BASEL, SWITZERLAND, Suiza
Tipo de documento: Article
Volumen: 14 Número: 12
Páginas:
WOS Id: 000904477400001
ID de PubMed: 36559138
imagen gold, Green Published

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