Analysis of the C9orf72 Gene in Patients with Amyotrophic Lateral Sclerosis in Spain and Different Populations Worldwide


Por: Garcia-Redondo, A, Dols-Icardo, O, Rojas-Garcia, R, Esteban-Perez, J, Cordero-Vazquez, P, Munoz-Blanco, JL, Catalina, I, Gonzalez-Munoz, M, Varona, L, Sarasola, E, Povedano, M, Sevilla, T, Guerrero, A, Pardo, J, de Munain, AL, Marquez-Infante, C, de Rivera, FJR, Pastor, P, Jerico, I, de Arcaya, AA, Mora, JS, Clarimon, J

Publicada: 1 ene 2013
Resumen:
A hexanucleotide repeat expansion in chromosome 9 open reading frame 72 (C9orf72) can cause amyotrophic lateral sclerosis (ALS) and/or frontotemporal dementia (FTD). We assessed its frequency in 781 sporadic ALS (sALS) and 155 familial ALS (fALS) cases, and in 248 Spanish controls. We tested the presence of the reported founder haplotype among mutation carriers and in 171 Ceph Europeans from Utah (CEU), 170 Yoruba Africans, 81 Han Chinese, and 85 Japanese subjects. The C9orf72 expansion was present in 27.1% of fALS and 3.2% of sALS. Mutation carriers showed lower age at onset (P = 0.04), shorter survival (P = 0.02), greater co-occurrence of FTD (P = 8.2 x 10(-5)), and more family history of ALS (P = 1.4 x 10(-20)), than noncarriers. No association between alleles within the normal range and the risk of ALS was found (P = 0.12). All 61 of the mutation carriers were tested and a patient carrying 28 hexanucleotide repeats presented with the founder haplotype. This haplotype was found in 5.6% Yoruba Africans, 8.9% CEU, 3.9% Japanese, and 1.6% Han Chinese chromosomes. Hum Mutat 34:79-82, 2013. (C) 2012 Wiley Periodicals, Inc.

Filiaciones:
Garcia-Redondo, A:
 Hosp 12 Octubre, Inst Invest Biomed, ALS Unit, Dept Neurol, E-28041 Madrid, Spain

 Ctr Biomed Network Res Rare Dis CIBERER, Valencia, Spain

Dols-Icardo, O:
 Hosp Santa Creu & Sant Pau, Dept Neurol, Barcelona 08025, Spain

 Ctr Networker Biomed Res Neurodegenerat Dis CIBER, Barcelona, Spain

Rojas-Garcia, R:
 Hosp Santa Creu & Sant Pau, Dept Neurol, Barcelona 08025, Spain

 Ctr Networker Biomed Res Neurodegenerat Dis CIBER, Barcelona, Spain

Esteban-Perez, J:
 Hosp 12 Octubre, Inst Invest Biomed, ALS Unit, Dept Neurol, E-28041 Madrid, Spain

 Ctr Biomed Network Res Rare Dis CIBERER, Valencia, Spain

Cordero-Vazquez, P:
 Hosp 12 Octubre, Inst Invest Biomed, ALS Unit, Dept Neurol, E-28041 Madrid, Spain

 Ctr Biomed Network Res Rare Dis CIBERER, Valencia, Spain

Munoz-Blanco, JL:
 Hosp Univ Gregorio Maranon, Dept Neurol, ALS Unit, Madrid, Spain

Catalina, I:
 Hosp Univ Gregorio Maranon, Dept Neurol, ALS Unit, Madrid, Spain

Gonzalez-Munoz, M:
 Hosp Carlos III, ALS Unit, Dept Immunol, Madrid, Spain

Varona, L:
 Hosp Univ Basurto, Dept Neurol, Bilbao, Spain

 Hosp Univ Basurto, Dept Genet, Bilbao, Spain

Sarasola, E:
 Hosp Univ Basurto, Dept Neurol, Bilbao, Spain

 Hosp Univ Basurto, Dept Genet, Bilbao, Spain

Povedano, M:
 Bellvitge Hosp, Dept Neurol, Barcelona, Spain

Sevilla, T:
 Hosp La Fe, Dept Neurol, E-46009 Valencia, Spain

Guerrero, A:
 Hosp Clin Univ San Carlos, ALS Unit, Madrid, Spain

Pardo, J:
 Clin Hosp Santiago Compostela, SERGAS, Dept Neurol, Santiago De Compostela, Spain

de Munain, AL:
 Ctr Networker Biomed Res Neurodegenerat Dis CIBER, Barcelona, Spain

 Hosp Univ Donostia, Dept Neurol, Neurosci Area, Biodonostia Hlth Res Inst, San Sebastian, Spain

Marquez-Infante, C:
 Hosp Univ Virgen del Rocio, Dept Neurol, Seville, Spain

de Rivera, FJR:
 Hosp Univ La Paz, Dept Neurol, ALS Unit, Madrid, Spain

Pastor, P:
 Ctr Networker Biomed Res Neurodegenerat Dis CIBER, Barcelona, Spain

 Univ Navarra Med Sch, Univ Navarra Clin, Ctr Appl Med Res, Neurogenet Lab,Div Neurosci, Pamplona, Spain

 Univ Navarra Med Sch, Univ Navarra Clin, Dept Neurol, Pamplona, Spain

Jerico, I:
 Complejo Hosp Navarra, Dept Neurol, Pamplona, Spain

de Arcaya, AA:
 Hosp Univ Araba Txagorritxu, Dept Neurol, Vitoria, Spain

Mora, JS:
 Hosp Carlos III, ALS Unit, Dept Neurol, Madrid, Spain

Clarimon, J:
 Hosp Santa Creu & Sant Pau, Dept Neurol, Barcelona 08025, Spain

 Ctr Networker Biomed Res Neurodegenerat Dis CIBER, Barcelona, Spain
ISSN: 10597794





HUMAN MUTATION
Editorial
WILEY, 111 RIVER ST, HOBOKEN 07030-5774, NJ USA, Estados Unidos America
Tipo de documento: Article
Volumen: 34 Número: 1
Páginas: 79-82
WOS Id: 000314476900011
ID de PubMed: 22936364

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